Glutaric aciduria type I: Outcome in the Republic of Ireland

Date

2004-11

Type

Article

Journal title

Journal of Inherited Metabolic Disease

Issue

Vol. 6 No. 27

Author(s)

Gomaa Sulaiman

Pages

917 - 920

Abstract

Twenty-onepatientshavebeendiagnosedwithglutaricaciduriatypeI over a 16-year period in the Republic of Ireland, 11 following clinical presentation and10followingahigh-riskscreen.Nineteenhavebeenmanagedwithdiet.Eight patients have died, of whom 7 were diagnosed clinically. Six had dystonic and one spastic cerebral palsy. Of the 11 patients who did not have cerebral palsy, 10werediagnosedfollowingahigh-riskscreen.Sevenofthe11havenoabnormal neurological signs; 6 of the 7 have abnormal CT or MRI findings; and no case of striataldegenerationhasoccurredduringthepast14yearsinthehigh-riskscreened group.

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